GAA Deficiency in Pompe Disease Is Alleviated by

GAA Deficiency in Pompe Disease Is Alleviated by Exon Inclusion in i. PSC-Derived Skeletal

GAA Deficiency in Pompe Disease Is Alleviated by Exon Inclusion in i. PSC-Derived Skeletal Muscle Cells Erik van der Wal, Atze J. Bergsma, Tom J. M. van Gestel, Stijn L. M. in ‘t Groen, Holm Zaehres, Marcos J. Araúzo-Bravo, Hans R. Schöler, Ans T. van der Ploeg, W. W. M. Pim Pijnappel Molecular Therapy - Nucleic Acids Volume 7 Pages 101 -115 (June 2017) DOI: 10. 1016/j. omtn. 2017. 03. 002 Copyright © 2017 The Author(s) Terms and Conditions

Figure 1 Molecular Therapy - Nucleic Acids 2017 7101 -115 DOI: (10. 1016/j. omtn.

Figure 1 Molecular Therapy - Nucleic Acids 2017 7101 -115 DOI: (10. 1016/j. omtn. 2017. 03. 002) Copyright © 2017 The Author(s) Terms and Conditions

Figure 2 Molecular Therapy - Nucleic Acids 2017 7101 -115 DOI: (10. 1016/j. omtn.

Figure 2 Molecular Therapy - Nucleic Acids 2017 7101 -115 DOI: (10. 1016/j. omtn. 2017. 03. 002) Copyright © 2017 The Author(s) Terms and Conditions

Figure 3 Molecular Therapy - Nucleic Acids 2017 7101 -115 DOI: (10. 1016/j. omtn.

Figure 3 Molecular Therapy - Nucleic Acids 2017 7101 -115 DOI: (10. 1016/j. omtn. 2017. 03. 002) Copyright © 2017 The Author(s) Terms and Conditions

Figure 4 Molecular Therapy - Nucleic Acids 2017 7101 -115 DOI: (10. 1016/j. omtn.

Figure 4 Molecular Therapy - Nucleic Acids 2017 7101 -115 DOI: (10. 1016/j. omtn. 2017. 03. 002) Copyright © 2017 The Author(s) Terms and Conditions

Figure 5 Molecular Therapy - Nucleic Acids 2017 7101 -115 DOI: (10. 1016/j. omtn.

Figure 5 Molecular Therapy - Nucleic Acids 2017 7101 -115 DOI: (10. 1016/j. omtn. 2017. 03. 002) Copyright © 2017 The Author(s) Terms and Conditions

Figure 6 Molecular Therapy - Nucleic Acids 2017 7101 -115 DOI: (10. 1016/j. omtn.

Figure 6 Molecular Therapy - Nucleic Acids 2017 7101 -115 DOI: (10. 1016/j. omtn. 2017. 03. 002) Copyright © 2017 The Author(s) Terms and Conditions

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